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Uppsala-Örebro Centre for Rare Diseases

The Finnish Network for Rare Diseases

Karolinska Center for Rare Diseases (Karolinska, Stockholm) Medical University Hospitals in Sweden

Centre for Rare Diseases in Southeast Region of Sweden

2 (Skåne, Lund) Medical University Hospitals, Sweden

John Walton Muscular Dystrophy Research Centre from University of Newcastle

Karolinska Institutet

Einstok Born

Vinnova

Karolinska Institute

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