Programme Committee

Programme Committee Co-Chairs

Name Affiliation(s) Country
Wills Hughes-Wilson Wills Hughes-Wilson
  • Vice President External Affairs, Chief Patient Access Officer, Swedish Orphan Biovitrum (sobi)
Sweden
Alastair Kent
  • Director, Genetic Alliance UK
UK
Bruno Sepodes
  • Chair COMP
  • Professor at the University of Lisbon, Portugal
Portugal

Programme Committee Members

Name Affiliation(s) Country
Kate Bushby Professor of Neuromuscular Genetics, Newcastle University UK
Dorica Dan President, Romanian Pader Willi Association Romania
Pascal Garel Chief Executive, European Hospital and Healthcare Federation (HOPE) Belgium
Adam Heathfield Co-Chair Task Force RDs & ODs of EFPIA- EuropaBio, Pfizer UK
Helena Kaariainen President ESHG, National Institute for Health and Welfare Finland
Kristina Larsson Head of Orphan Medicines, EMA EU
yann-lecam Yann Le Cam Chief Executive Officer, EURORDIS France
Jordi Llinares Garcia Head of Product Development Scientific Support Department, EMA EU
Kay Parkinson Alström Europe UK
Vinciane Pirard Co-Chair Task Force RDs & ODs of EFPIA-EuropaBio, Genzyme Netherlands
Liz Porterfield Head, Strategic Planning/Clinical Priorities, The Scottish Government UK
 Gayatri Rao Gayatri Rao Director, FDA’s Office of Orphan Products Development (OOPD) USA
Ana Rath Director, Orphanet France
 Miriam Schlangen Miriam Schlangen Head of Coordinating Office of the National League (NAMSE) Germany
Domenica Taruscio Director, ISTITUTO SUPERIORE DI SANTA (ISS) Italy
Till_Voigtlander Till Voigtländer Clinical Institute of Neurology, Medical University of Vienna Austria
flaminia_macchia Flaminia Macchia EUCOPE Member, Director EU Government Affairs & Public Policy

Vertex Pharmaceuticals

UK